This is a Phase 1/2 multicenter, open-label, single dose trial of 4D-710 investigational gene therapy in adults with cystic fibrosis.
- Investigator
- Cesar A Trillo-Alvarez
- Status
- Accepting Candidates
- Ages
- 18 Years - N/A
- Sexes
- All
Research at a glance
Top areas of exploration
- Acute Lung Injury , 2 publications
- Respiratory Distress Syndrome , 2 publications
- Critical Illness , 2 publications
- Anti-Bacterial Agents , 1 publications
Research activity
Active clinical trials
The purpose of this study is to evaluate the safety, and tolerability and efficacy of VX-522 in participants 18 years of age and older with cystic fibrosis and a cystic fibrosis transmembrane conductance regulator (CFTR) genotype not responsive to…
- Investigator
- Cesar A Trillo-Alvarez
- Status
- Accepting Candidates
- Ages
- 18 Years - 64 Years
- Sexes
- All
My publications
Filter publications
12 publications
2024
A Randomized Clinical Trial of Bayesian-Guided Beta-Lactam Infusion Strategy and Associated Bacterial Resistance and Clinical Outcomes in Patients With Severe Pneumonia.
Therapeutic drug monitoring
•2021
CFTR modulator use in post lung transplant recipients
The Journal of Heart and Lung Transplantation
2021
Ustekinumab associated chronic eosinophilic pneumonia.
The Journal of asthma : official journal of the Association for the Care of Asthma
•2019
Multidisciplinary Care for Cystic Fibrosis Liver Disease: Where Does the Adult Hepatologist Fit In?
Clinical liver disease
•2018
Risk factors for hepatic steatosis in adults with cystic fibrosis: Similarities to non-alcoholic fatty liver disease.
World journal of hepatology
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