This is a Phase 1/2 multicenter, open-label, single dose trial of 4D-710 investigational gene therapy in adults with cystic fibrosis.
- Investigator
- Cesar A Trillo-Alvarez
- Status
- Accepting Candidates
- Ages
- 18 Years - N/A
- Sexes
- All
Critical Care Medicine Specialist, Pulmonologist (Lung Specialist)
This is a Phase 1/2 multicenter, open-label, single dose trial of 4D-710 investigational gene therapy in adults with cystic fibrosis.
The purpose of this study is to evaluate the safety, and tolerability and efficacy of VX-522 in participants 18 years of age and older with cystic fibrosis and a cystic fibrosis transmembrane conductance regulator (CFTR) genotype not responsive to…
12 publications
2011
The European respiratory journal
•2011
Chest
•2011
Respiratory care
•2011
BMJ open
•2010
BMC emergency medicine
•