LUMINA
This study is a placebo-controlled Phase I study to evaluate the safety, tolerability, pharmacokinetics, and pharmacodynamics of the antisense oligonucleotide (ASO) AMX0114 in adult participants with amyotrophic lateral sclerosis (ALS).
- Investigator
- James Wymer
- Status
- Accepting Candidates
- Ages
- 18 Years - N/A
- Sexes
- All
ALS Imaging
- Investigator
- James Wymer
- Status
- Accepting Candidates
Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy
The purpose of this study is to evaluate the efficacy, safety, tolerability and pharmacokinetics of NMD670 in the treatment of ambulatory adults with spinal muscular atrophy type 3
- Investigator
- James Wymer
- Status
- Accepting Candidates
- Ages
- 18 Years - 75 Years
- Sexes
- All
