2012
Pom-001 Phase 1/2 Study of Bmn 701, Gilt-Tagged Recombinant Human (Rh) Gaa in Late-Onset Pompe Disease: Preliminary Report
Molecular Genetics and Metabolism
Hospitalist
24 publications
2012
Molecular Genetics and Metabolism
2010
Pediatrics in review
•2010
The Journal of pediatrics
•2009
Case reports in medicine
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