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Barry J Byrne, MD, PhD

Pediatric Cardiologist

Photo of Barry J Byrne

Research at a glance

Top areas of exploration

  • Genetic Therapy , 86 publications
  • Genetic Vectors , 80 publications
  • Glycogen Storage Disease Type II , 60 publications
  • Muscle, Skeletal , 41 publications

Research activity

368 publications

22,468 citations

Why is this important?

Active clinical trials

My publications

368 publications

2024

104-week efficacy and safety of cipaglucosidase alfa plus miglustat in adults with late-onset Pompe disease: a phase III open-label extension study (ATB200-07).

Journal of neurology

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2024

B cell focused transient immune suppression protocol for efficient AAV readministration to the liver.

Molecular therapy. Methods & clinical development

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2024

Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe disease.

Frontiers in neurology

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2024

Codon-Optimized and de novo-Synthesized E-Selectin/AAV2 Dose-Response Study for Vascular Regeneration Gene Therapy.

Annals of surgery

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2024

Corrigendum: Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe disease.

Frontiers in neurology

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